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Antisense oligonucleotide- and CRISPR-Cas9-mediated rescue of mRNA splicing for a deep intronic CLRN1 mutation
Antisense oligonucleotide- and CRISPR-Cas9-mediated rescue of mRNA splicing for a deep intronic CLRN1 mutation
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Panagiotopoulos, Anna-Lena
2021
English
Universitätsbibliothek der Ludwig-Maximilians-Universität München
Panagiotopoulos, Anna-Lena (2021): Antisense oligonucleotide- and CRISPR-Cas9-mediated rescue of mRNA splicing for a deep intronic CLRN1 mutation. Dissertation, LMU München: Faculty of Veterinary Medicine
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